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Terminated Phase 2 Interventional Results available

Study to Assess the Effects of PTC857 Treatment in Participants With Amyotrophic Lateral Sclerosis ALS

ClinicalTrials.gov ID: NCT05349721

Public ClinicalTrials.gov record NCT05349721. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 20, 2026, 4:24 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Phase 2, Randomized, Double-Blind, Placebo-Controlled, Parallel Study to Assess the Efficacy, Safety, Tolerability, PK, and Biomarker Effects of PTC857 in Adult Subjects With Amyotrophic Lateral Sclerosis (CARDINALS)

Study identification

NCT ID
NCT05349721
Recruitment status
Terminated
Study type
Interventional
Phase
Phase 2
Lead sponsor
PTC Therapeutics
Industry
Enrollment
336 participants

Conditions and interventions

Interventions

  • PTC857 Drug
  • Placebo Drug

Drug

Eligibility (public fields only)

Age range
18 Years to 80 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
May 14, 2022
Primary completion
Sep 25, 2024
Completion
Jan 29, 2025
Last update posted
Jul 31, 2025

2022 – 2025

United States locations

U.S. sites
14
U.S. states
10
U.S. cities
14
Facility City State ZIP Site status
UC Irvine Health ALS and Neuromuscular Center Orange California 92868
Forbes Norris MDA/ALS Research Center at California Pacific Medical Center San Francisco California 94109
Holy Cross Hospital, Phil Smith Neuroscience Institute Fort Lauderdale Florida 33308
University of South Florida - Carol and Frank Morsani Center for Advanced Healthcare Tampa Florida 33612
Augusta University Augusta Georgia 30912
University of Kansas Medical Center (KUMC) - Landon Center on Aging Kansas City Kansas 66205
Henry Ford Health System Department of Neurology Detroit Michigan 48202
Neurology Associates, P.C. / Somnos Clinical Research Lincoln Nebraska 68506
University of Nebraska Medical Center Omaha Nebraska 68198-8440
Providence Brain and Spine Institute Portland Oregon 97213
Lewis Katz School of Medicine at Temple Universtiy Philadelphia Pennsylvania 19140
National Neuromuscular Research Institute Austin Texas 78759
Nerve and Muscle Center of Texas Houston Texas 77030
Medical College of Wisconsin Milwaukee Wisconsin 53226

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 41 non-U.S. sites.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT05349721, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jul 31, 2025 · Synced May 20, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT05349721 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →