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No Longer Available No phase listed Expanded access

Expanded Access Protocol to Provide Patisiran to Patients With Transthyretin-mediated Amyloidosis With Cardiomyopathy

ClinicalTrials.gov ID: NCT05505838

Public ClinicalTrials.gov record NCT05505838. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Jul 21, 2026, 6:52 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Expanded Access Protocol to Provide Patisiran to Patients With Transthyretin-mediated Amyloidosis (ATTR Amyloidosis) With Cardiomyopathy

Study identification

NCT ID
NCT05505838
Recruitment status
No Longer Available
Study type
Expanded access
Phase
Not listed
Lead sponsor
Alnylam Pharmaceuticals
Industry
Enrollment
Not listed

Conditions and interventions

Eligibility (public fields only)

Age range
18 Years to 85 Years
Sex
All
Healthy volunteers
Not listed

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Not listed
Primary completion
Not listed
Completion
Not listed
Last update posted
Feb 15, 2024

United States locations

U.S. sites
20
U.S. states
17
U.S. cities
20
Facility City State ZIP Site status
Mayo Clinic Hospital Phoenix Arizona 85054
Cedars-Sinai Medical Center Los Angeles California 90048
University of California San Diego San Diego California 92093
Mayo Clinic Florida Jacksonville Florida 32224
University of Chicago Chicago Illinois 60637
NorthShore University Evanston Illinois 60201
Indiana University Health Hospital Indianapolis Indiana 46202
The University of Kansas Medical Center Kansas City Kansas 66160
The Johns Hopkins University Baltimore Maryland 21205
Boston University Boston Massachusetts 02118
Mayo Clinic Rochester Minnesota 55905
Washington University St Louis Missouri 63110
University of Nebraska Medical Center Omaha Nebraska 68198
Columbia University Irving Medical Center New York New York 10032
Cleveland Clinic Cleveland Ohio 44195
OhioHealth Research Institute Columbus Ohio 43214
Penn Presbyerian Medical Center Philadelphia Pennsylvania 19104
Vanderbilt University Nashville Tennessee 37232
Baylor Scott & White Research Institute Dallas Texas 75204
University of Utah Salt Lake City Utah 84112

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT05505838, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Feb 15, 2024 · Synced Jul 21, 2026

Related: full search, browse by condition, browse by drug or therapy, browse by sponsor, browse by U.S. city.

Open the official record

The complete protocol, eligibility criteria, and contact information for NCT05505838 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →