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Recruiting No phase listed Observational

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

ClinicalTrials.gov ID: NCT05813678

Public ClinicalTrials.gov record NCT05813678. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Aug 5, 2026, 2:00 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Multi-Center, Observational Study to Evaluate the Long-Term Safety of Subcutaneous Injections of Palynziq® (Pegvaliase) in Subjects With Phenylketonuria

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

This is a 10-year multi-center, global, observational study to further characterize the safety profile of pegvaliase, including hypersensitivity reactions, long-term safety and tolerability, and the effectiveness of the additional risk minimization measures (aRMMs) (European Union (EU) only) in subjects receiving pegvaliase for the treatment of PKU. Subjects for whom a clinical decision has been made that they will receive pegvaliase to treat their PKU within 30 days following the date of enrollment (incident-users) or have previously started treatment with pegvaliase at the date of enrollment (prevalent-users) are eligible for participation in this study.

Study identification

NCT ID
NCT05813678
Recruitment status
Recruiting
Study type
Observational
Phase
Not listed
Lead sponsor
BioMarin Pharmaceutical
Industry
Enrollment
450 participants

Conditions and interventions

Interventions

Drug

Eligibility (public fields only)

Age range
Not listed
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jun 5, 2022
Primary completion
Oct 31, 2033
Completion
Oct 31, 2033
Last update posted
Mar 24, 2026

2022 – 2033

United States locations

U.S. sites
12
U.S. states
12
U.S. cities
12
Facility City State ZIP Site status
University of Colorado Aurora Colorado 80045 Recruiting
Emory University Atlanta Georgia 30322 Recruiting
Northwestern University Chicago Illinois 60611 Recruiting
Indiana University School of Medicine Indianapolis Indiana 46202 Recruiting
Tulane University Medical Center New Orleans Louisiana 70118 Recruiting
Boston Children's Hospital Boston Massachusetts 02215 Recruiting
Oregon Health and Science University Portland Oregon 97239 Recruiting
University of Pittsburgh Medical Center Pittsburgh Pennsylvania 15224 Recruiting
Vanderbilt University Medical School Nashville Tennessee 37235 Recruiting
University of Texas Southwestern Medical Center Dallas Texas 75390 Recruiting
University of Utah Salt Lake City Utah 84112 Recruiting
Medical College of Wisconsin Milwaukee Wisconsin 53226 Recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

Non-U.S. locations

This page focuses on the U.S. directory. The official record also lists 14 non-U.S. sites.

Recently updated Phenylketonuria (PKU) trials

Other public records listing Phenylketonuria (PKU). Sorted by last update posted; newest first. Not a recommendation.

All Phenylketonuria (PKU) trials →

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT05813678, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Mar 24, 2026 · Synced Aug 5, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT05813678 live on ClinicalTrials.gov.

View official ClinicalTrials.gov record →