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Recruiting No phase listed Observational

VIrtual STudy in Achondroplasia for the US (VISTA)

ClinicalTrials.gov ID: NCT06168201

Public ClinicalTrials.gov record NCT06168201. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced Sep 6, 2026, 10:06 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

This is an observational study of individuals with achondroplasia in the United States. The primary study population consists of pediatric individuals treated and untreated with VOXZOGO™. Study enrollment started in February 2023. The projected total duration of the study is approximately 5 years at minimum from start of study recruitment in February 2023, with the duration of individual prospective follow-up differing depending on the time of enrollment. The study duration may be extended based on decisions by the study sponsor. Data will be collected in two formats for the primary pediatric study population: 1. Participant-mediated access to electronic health records(including medical imaging, when available) which will enable retrospective and prospective collection of secondary data reflecting real-life treatment use and clinical care. . 2. Primary data collection of Clinical Outcome Assessments (COAs) and questionnaire data. Data will be collected in the following format for the adult cohort: \- Participant-mediated access to electronic health records (including medical imaging, when available) which will enable retrospective and prospective collection of secondary data reflecting real-life treatment use and clinical care. The primary study population will include approximately 150 pediatric individuals with achondroplasia regardless of their treatment status with VOXZOGO™. Individuals may change status from untreated to treated during the prospective period of the study (or vice versa) however they will only be counted once, based on their treated status at the point of enrollment. The secondary study population will include 20 adolescent and adult participants.

Study identification

NCT ID
NCT06168201
Recruitment status
Recruiting
Study type
Observational
Phase
Not listed
Lead sponsor
BioMarin Pharmaceutical
Industry
Enrollment
170 participants

Conditions and interventions

Conditions

Interventions

Not listed

Eligibility (public fields only)

Age range
0 Months to 18 Years
Sex
All
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Feb 20, 2023
Primary completion
Jan 31, 2028
Completion
Jan 31, 2028
Last update posted
Jun 29, 2026

2023 – 2028

United States locations

U.S. sites
8
U.S. states
7
U.S. cities
8
Facility City State ZIP Site status
UCSF Oakland California 94609 Recruiting
PicnicHealth San Francisco California 94107 Recruiting
Johns Hopkins University (JHU) Baltimore Maryland 21205 Recruiting
Piedmont Health Statesville North Carolina 28625 Recruiting
University of Cincinnati Cincinnati Ohio 45229 Recruiting
Sanford Health Sioux Falls South Dakota 57115 Recruiting
Baylor College of Medicine Houston Texas 77030-2316 Recruiting
University of Wisconsin Madison Wisconsin 53726 Recruiting

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT06168201, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Jun 29, 2026 · Synced Sep 6, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT06168201 live on ClinicalTrials.gov.

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