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Enrolling by invitation No phase listed Observational

A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice

ClinicalTrials.gov ID: NCT06606340

Public ClinicalTrials.gov record NCT06606340. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

ClinicalTrials.gov public records Last synced May 11, 2026, 4:32 PM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

A Long-term Observational Study Evaluating Sarepta Therapeutics, Inc.'s Exon-Skipping Therapies in Patients With Duchenne Muscular Dystrophy Under Conditions of Routine Clinical Practice

Study identification

NCT ID
NCT06606340
Recruitment status
Enrolling by invitation
Study type
Observational
Phase
Not listed
Lead sponsor
Sarepta Therapeutics, Inc.
Industry
Enrollment
300 participants

Conditions and interventions

Interventions

  • Casimersen Drug
  • Eteplirsen Drug
  • Golodirsen Drug

Drug

Eligibility (public fields only)

Age range
Not listed
Sex
Male
Healthy volunteers
Healthy volunteers not accepted

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date
Jan 6, 2019
Primary completion
Dec 30, 2033
Completion
Dec 30, 2033
Last update posted
Sep 9, 2025

2019 – 2033

United States locations

U.S. sites
20
U.S. states
14
U.S. cities
20
Facility City State ZIP Site status
Arkansas Children's Hospital Research Institute Little Rock Arkansas 72202
Children's Hospital Los Angeles Los Angeles California 90027
University of California Davis Medical Center Sacramento California 95817
Children's National Hospital Washington D.C. District of Columbia 20010
University of Florida Gainesville Florida 32610
University Of Iowa Hospitals And Clinics Iowa City Iowa 52242
Kennedy Krieger Institute Baltimore Maryland 21287
Washington University St Louis Missouri 63110
Columbia University Medical Center - PIN New York New York 10032
Duke Lenox Baker Children's Hospital Durham North Carolina 27705
Atrium Health Wake Forest University Health Sciences Winston-Salem North Carolina 27157
Children's Hospital Medical Center Cincinnati Ohio 45229
Nationwide Children's Hospital Columbus Ohio 43205
Penn State Health Milton S. Hershey Medical Center Hershey Pennsylvania 17033-0850
Children's Hospital of Philadelphia Philadelphia Pennsylvania 19104
UPMC Children's Hospital of Pittsburgh Pittsburgh Pennsylvania 15213
Cook Children's Hospital Fort Worth Texas 76104
Texas Children's Hospital Houston Texas 77030
UVA Children's Hospital Charlottesville Virginia 22908
Seattle Children's Hospital Seattle Washington 98105

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows
Public field values for ClinicalTrials.gov record NCT06606340, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do
No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from
Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh
Last update posted Sep 9, 2025 · Synced May 11, 2026

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Open the official record

The complete protocol, eligibility criteria, and contact information for NCT06606340 live on ClinicalTrials.gov.

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