Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 Skipping

ClinicalTrials.gov ID: NCT07250737

Public ClinicalTrials.gov record NCT07250737. Field values are reproduced from the official study page; the official ClinicalTrials.gov record remains the source of truth for eligibility, enrollment, and contact information.

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ClinicalTrials.gov public records Last synced Sep 11, 2026, 4:00 AM EDT

Data is sourced from official ClinicalTrials.gov public API records. Always review the official ClinicalTrials.gov record for the latest information.

Official title

Managed Access to Investigational Use of AOC 1044 in Participants With DMD Mutations Amenable to Exon 44 Skipping

Brief summary

Reproduced verbatim from the official ClinicalTrials.gov record. Not medical advice.

The purpose of this Managed Access Program is to allow access to delpacibart zotadirsen (AOC 1044) for eligible patients diagnosed with DMD mutations amenable to exon 44 skipping. The patient's Administering Physician should follow the suggested treatment guidelines and comply with all local health authority regulations.

Study identification

NCT ID: NCT07250737
Recruitment status: Available
Study type: Expanded access
Phase: Not listed
Lead sponsor: Avidity Biosciences, Inc.; Industry
Enrollment: Not listed

Conditions and interventions

Conditions

Interventions

delpacibart zotadirsen Drug

Drug

Eligibility (public fields only)

Age range: 2 Years and older
Sex: Male
Healthy volunteers: Not listed

This page does not interpret eligibility. Detailed inclusion and exclusion criteria are on the official ClinicalTrials.gov record.

Study timeline

Start date: Not listed
Primary completion: Not listed
Completion: Not listed
Last update posted: Aug 31, 2026

United States locations

U.S. sites: 21
U.S. states: 17
U.S. cities: 20

Facility	City	State	ZIP	Site status
University of Alabama	Birmingham	Alabama	35294	Available
Arkansas Children's Hospital	Little Rock	Arkansas	72202	Available
UCI Alpha Clinic	Irvine	California	92612	Available
Lucille Packard Children's Hospital at Stanford	San Carlos	California	94070	Available
UC San Diego Health	San Diego	California	92121	Available
Connecticut Children's Medical Center	Hartford	Connecticut	06106	Available
Rare Disease Research	Kissimmee	Florida	34746	Available
Nicklaus Children's Hospital	Miami	Florida	33155	Available
Rare Disease Research	Atlanta	Georgia	30329	Available
University of Kansas Medical Center	Kansas City	Kansas	66103	Available
UMass Memorial Health Care	Worcester	Massachusetts	01583	Available
Gillette Children's	Saint Paul	Minnesota	55101	Available
Washington University	St Louis	Missouri	63110	Available
Rare Disease Research	Iselin	New Jersey	08830	Available
Rare Disease Research	Hillsborough	North Carolina	27278	Available
Nationwide Children's Hospital	Columbus	Ohio	43205	Available
Children's Hospital of Philadelphia	Philadelphia	Pennsylvania	19104	Available
University of Pennsylvania	Philadelphia	Pennsylvania	19104	Available
Prisma Health-Midlands Children's Hospital	Columbia	South Carolina	29203	Available
Neurology & Neuromuscular Care Center	Flower Mound	Texas	75028	Available
University of Vermont Medical Center	Burlington	Vermont	05401	Available

Site contact phone numbers, emails, and investigator names are intentionally not displayed here. Open the official ClinicalTrials.gov record for site contact information.

About this trial record page

What this page shows: Public field values for ClinicalTrials.gov record NCT07250737, including study identification, conditions, interventions, eligibility (age, sex, healthy volunteer), timeline, and U.S. site list.
What this page does not do: No medical advice, eligibility judgments, treatment recommendations, study quality scoring, or AI-generated medical summaries. No site contact phone numbers, emails, or investigator names.
Where the data comes from: Sourced from the official ClinicalTrials.gov public API. The official record is the source of truth.
Last refresh: Last update posted Aug 31, 2026 · Synced Sep 11, 2026

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The complete protocol, eligibility criteria, and contact information for NCT07250737 live on ClinicalTrials.gov.

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